cerdelga
sanofi b.v. - eliglustat - gaucher disease - other alimentary tract and metabolism products, - cerdelga is indicated for the long-term treatment of adult patients with gaucher disease type 1 (gd1), who are cyp2d6 poor metabolisers (pms), intermediate metabolisers (ims) or extensive metabolisers (ems).
cerdelga 84mg capsules
sanofi - eliglustat tartrate - capsule - 84.4mg
cerdelga
sanofi israel ltd - eliglustat - hard capsule - eliglustat 84.4 mg - eliglustat - cerdelga is indicated for the long-term treatment of adult patients with gaucher disease type 1 (gd1), who are cyp2d6 poor metabolisers (pms), intermediate metabolisers (ims) or extensive metabolisers (ems).
givlaari
alnylam netherlands b.v. - givosiran - porphyrias, hepatic - various alimentary tract and metabolism products - treatment of acute hepatic porphyria (ahp) in adults and adolescents aged 12 years and older.
cufence 200 mg
mbi pharma ltd., israel - trientine as dihydrochloride - hard capsule - trientine as dihydrochloride 200 mg - trientine - cufence is indicated for the treatment of wilson’s disease in patients intolerant to d-penicillamine therapy, in adults, adolescents and children aged 5 years or older.
oxlumo
alnylam netherlands b.v. - lumasiran sodium - hyperoxaluria, primary - other alimentary tract and metabolism products, - treatment of primary hyperoxaluria type 1 (ph1) in all age groups.
dojolvi liquid
ultragenyx pharmaceutical inc - triheptanoin - liquid - 100% - triheptanoin 100% - caloric agents
givlaari
medison pharma ltd - givosiran as sodium - solution for injection - givosiran as sodium 189 mg / 1 ml - givosiran - givlaari is indicated for the treatment of acute hepatic porphyria (ahp) in adults and adolescents aged 12 years and older
trientine 167 mg hard capsules
tillomed pharma gmbh - trientine dihydrochloride - capsule, hard - trientine
nulibry
tmc pharma (eu) limited - fosdenopterin hydrobromide dihydrate - metal metabolism, inborn errors - other alimentary tract and metabolism products, - nulibry is indicated for the treatment of patients with molybdenum cofactor deficiency (mocd) type a.