European Union - English - EMA (European Medicines Agency)

alexion europe sas - asfotase alfa - hypophosphatasia - other alimentary tract and metabolism products, - strensiq is indicated for long-term enzyme replacement therapy in patients with paediatric-onset hypophosphatasia to treat the bone manifestations of the disease.

European Union - English - EMA (European Medicines Agency)

biomarin international limited - cerliponase alfa - neuronal ceroid-lipofuscinoses - other alimentary tract and metabolism products, - brineura is indicated for the treatment of neuronal ceroid lipofuscinosis type 2 (cln2) disease, also known as tripeptidyl peptidase 1 (tpp1) deficiency,

European Union - English - EMA (European Medicines Agency)

amicus therapeutics europe limited - cipaglucosidase alfa - glycogen storage disease type ii - other alimentary tract and metabolism products, - pombiliti (cipaglucosidase alfa) is a long-term enzyme replacement therapy used in combination with the enzyme stabiliser miglustat for the treatment of adults with late-onset pompe disease (acid α-glucosidase [gaa] deficiency).

European Union - English - EMA (European Medicines Agency)

biomarin international limited - recombinant human n-acetylgalactosamine-6-sulfatase - mucopolysaccharidosis iv - other alimentary tract and metabolism products, - vimizim is indicated for the treatment of mucopolysaccharidosis, type iva (morquio a syndrome, mps iva) in patients of all ages.

Canada - English - Health Canada

biomarin international limited - elosulfase alfa - solution - 1mg - elosulfase alfa 1mg - enzymes

United Kingdom - English - MHRA (Medicines & Healthcare Products Regulatory Agency)

alexion pharma uk ltd - asfotase alfa - solution for injection - 40mg/1ml

United Kingdom - English - MHRA (Medicines & Healthcare Products Regulatory Agency)

alexion pharma uk ltd - asfotase alfa - solution for injection - 40mg/1ml

United Kingdom - English - MHRA (Medicines & Healthcare Products Regulatory Agency)

alexion pharma uk ltd - asfotase alfa - solution for injection - 40mg/1ml

United Kingdom - English - MHRA (Medicines & Healthcare Products Regulatory Agency)

alexion pharma uk ltd - asfotase alfa - solution for injection - 100mg/1ml

European Union - English - EMA (European Medicines Agency)

chiesi farmaceutici s.p.a. - velmanase alfa - alpha-mannosidosis - other alimentary tract and metabolism products, - treatment of non-neurological manifestations in patients with mild to moderate alpha-mannosidosis.,