roche registration gmbh - risdiplam - muskelatrofi, spinal - andre midler mod forstyrrelser i muskel-skeletsystemet - evrysdi is indicated for the treatment of 5q spinal muscular atrophy (sma) in patients with a clinical diagnosis of sma type 1, type 2 or type 3 or with one to four smn2 copies.
ipsen pharma - palovarotene - myositis ossificans - andre midler mod forstyrrelser i muskel-skeletsystemet - treatment of fibrodysplasia ossificans progressiva.